NEWS

Access to Gene Therapies
Access to gene therapies has changed the healthcare landscape. Gene therapies are a field of study for researchers and, at the same...

Rare Diseases in Global Health
Rare Diseases Worldwide This year, People Living With a Rare Disease (PLWRD) have a chance to get the recognition they deserve in...

G-BA resolutions on afamelanotide for the rare disease erythropoietic protoporphyria RAPS EURO Convergence Europe in Berlin on 7 May 2024
Obstacles for patient access to medicines can happen at different stages of a medicine's life cycle. Therefore, marketing...

Benefit assessment in Germany – G-BA resolutions on Zolgensma Market Access Day in Paris on 2 October 2023
The global community of market access professionals met in France on 2 October 2023 at the Market Access Day – the first...

Spesolimab: Does the benefit assessment of medicines for rare diseases need more flexibility? The case of spesolimab (Spevigo®)
After Boehringer Ingelheim’s announcement to withdraw a medicine for the treatment of a rare skin disease from the German market on...